Safety of lenadogene nolparvovec gene therapy over 5 years in 189 patients with Leber hereditary optic neuropathy
Vignal-ClermoḤ, Catherine, Patrick Yu-Wai-Man, Nancy Newman, Valerio Carelli, Mark Moster, Valérie Biousse, Prem Subramanian, et al. 2022. “Safety of Lenadogene Nolparvovec Gene Therapy over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy”. Am J Ophthalmol.